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Arcturus Therapeutics to Host a Key Opinion Leader Call on Ornithine Transcarbamylase (OTC) Deficiency on December 11SAN DIEGO, Dec. 03, 2018 (GLOBE NEWSWIRE) -- Arcturus Therapeutics Ltd. (NASDAQ: ARCT), a leading RNA medicines company focused on the development and commercialization of therapeutics towards rare, infectious, fibrotic, and respiratory diseases with significant unmet medical need, today announced that it will host a Key Opinion Leader (KOL) call for the investment community on current treatment options for ornithine transcarbamylase (OTC) deficiency on Tuesday, December 11 at 2:00 pm Eastern/11:00 am Pacific. The call will feature a presentation by key opinion leader Annette Feigenbaum, MBChB, FRCP, DABMG, from the University of California - San Diego, who will discuss the disease pathogenesis, manifestation, natural history and current treatment options for ornithine transcarbamylase (OTC) deficiency. Dr. Feigenbaum will be available to answer questions at the conclusion of the call. Dr. Pad Chivukula, Chief Scientific Officer of Arcturus Therapeutics, will also provide a brief overview of the company's ongoing LUNAR-OTC program, which utilizes the company's proprietary LUNAR® delivery platform to safely and effectively deliver OTC mRNA to liver cells, resulting in restoration of disease markers to normal levels. Annette Feigenbaum, MBChB, FRCP, DABMG, is an associate physician at Rady Children’s Hospital and University of California, San Diego, in the Department of Pediatrics and Biochemical Genetics. Her expertise is in the investigation, diagnosis, and management of inborn errors of metabolism, with a specific area of interest in urea cycle diseases. Dr. Feigenbaum qualified as a pediatrician in South Africa, followed by fellowships in clinical and biochemical genetics and research at the Hospital for Sick Children (SickKids) in Ontario, Canada, before being appointed as a staff physician in the Division of Clinical and Biochemical Genetics at SickKids. She continues as a part-time project investigator in the Department of Pediatrics and Research Institute at SickKids. She also serves as an associate professor at the University of Toronto. Dr. Feigenbaum has been site Principal Investigator for multiple clinical research studies in urea cycle diseases, PKU, and mitochondrial disease. She is certified in medical biochemical genetics by the American Board and the Canadian College of Medical Genetics.
Founded in 2013 and based in San Diego, California, Arcturus Therapeutics Ltd. (NASDAQ: ARCT) is an RNA medicines company with enabling technologies – UNA Oligomer chemistry and LUNAR® lipid-mediated delivery. Arcturus’ diverse pipeline of RNA therapeutics includes programs pursuing rare diseases, Hepatitis B, non-alcoholic steatohepatitis (NASH), cystic fibrosis, and vaccines. Arcturus’ versatile RNA therapeutics platforms can be applied toward multiple types of RNA medicines including small interfering RNA, messenger RNA, replicon RNA, antisense RNA, microRNA and gene editing therapeutics. Arcturus owns LUNAR lipid-mediated delivery and Unlocked Nucleomonomer Agent (UNA) technology including UNA Oligomers, which are covered by its extensive patent portfolio (140 patents and patent applications, issued in the U.S., Europe, Japan, China and other countries). Arcturus’ proprietary UNA technology can be used to target individual genes in the human genome, as well as viral genes, and other species for therapeutic purposes. Arcturus’ commitment to the development of novel RNA therapeutics has led to partnerships with Janssen Pharmaceuticals, Inc., part of the Janssen Pharmaceutical Companies of Johnson & Johnson, Ultragenyx Pharmaceutical, Inc., Takeda Pharmaceutical Company Limited, Synthetic Genomics Inc., CureVac AG and the Cystic Fibrosis Foundation. For more information, visit www.Arcturusrx.com, the content of which is not incorporated herein by reference. Forward-Looking Statements Contact Arcturus Investor Contacts |