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Abeona Therapeutics to Present Data for ABO-401 in Cystic Fibrosis and Retinal Disorders at the American Society of Gene and Cell Therapy Annual MeetingNEW YORK and CLEVELAND, April 15, 2019 (GLOBE NEWSWIRE) -- Abeona Therapeutics Inc. (Nasdaq: ABEO), a fully-integrated leader in gene and cell therapy, today announced that new data demonstrating the capabilities of the AIM™ capsid library in cystic fibrosis and retinal disorders will be presented at the American Society of Gene and Cell Therapy 22nd Annual Meeting, being held April 29 – May 2, 2019 in Washington, D.C. Additional preclinical data for ABO-202, the Company’s AAV9-based gene therapy for the treatment of patients with CLN1 disease, will also be presented. “The data to be presented at the ASGCT meeting will highlight study results on the delivery and expression of hCFTR gene in cystic fibrosis and the potential of the AIM™ AAV vector platform in the treatment of multiple retinal disorders. New data from IND-enabling studies of our program in CLN1 disease, expected to enter the clinic later this year, will also be presented,” said João Siffert, M.D., Chief Executive Officer. “The AIM capsid library has demonstrated significant versatility with the ability to deliver genes to target tissues with enhanced specificity,” added Timothy J. Miller, Ph.D., President and Chief Scientific Officer. “This next-generation AAV capsid platform has the potential to transform how we can target pulmonary, retinal and neurological disorders with gene therapy.” Identification of AAV Developed for Cystic Fibrosis (CF) Gene Therapy That Restores CFTR Function in Human CF Patient Cells Novel AAV Capsids Demonstrate Strong Retinal Expression in Non-Human Primates After Intravitreal Administration Intrathecal and Intravenous Combination Gene Therapy in the Mouse Model of Infantile Neuronal Ceroid Lipofuscinosis Extends Lifespan and Improves Behavioral Outcomesin Moderately Affected Mice Date/Time: Monday April 29, 11:45 a.m. – 12:00 p.m. ET Session title: Tools, Delivery and Neuro Capsids Room: Monroe About Abeona Therapeutics Forward Looking Statement Actual results may differ materially from those indicated by such forward-looking statements as a result of various important factors, numerous risks and uncertainties, including but not limited to: continued interest in our rare disease portfolio, our ability to initiate and enroll patients in clinical trials, the impact of competition, the ability to secure licenses for any technology that may be necessary to commercialize our products, the ability to achieve or obtain necessary regulatory approvals, the impact of changes in the financial markets and global economic conditions, risks associated with data analysis and reporting, and other risks as may be detailed from time to time in the Company’s annual reports on Form 10-K and quarterly reports on Form 10-Q and other reports filed by the Company with the Securities and Exchange Commission. The Company undertakes no obligation to revise the forward-looking statements or update them to reflect events or circumstances occurring after the date of this presentation, whether as a result of new information, future developments or otherwise, except as required by the federal securities laws. Investor Contact: Media Contact: |